Acknowledgments

This work was supported by funding from the University of Pennsylvania. Instruments supported by the National Science Foundation and the National Institutes of Health including HRMS (NIH RR-023444) and MALDI-MS (NSF MRI-0820996). S.A.B. wishes to thank the NIH for funding through the Chemistry-Biology Interface Training Program (T32 GM07133). We thank Professor Ashani Weeraratna, Amanpreet Kaur, and Professor Rugang Zhang for the cell lines and advice on cell culture. We also thank the Wistar Molecular Screening Facility for assistance.

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Chapter 3 : Triptycene-based small molecules modulate (CAG) · (CTG) repeat